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β-Thalassemia | Genetics in Medicine
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
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PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar
Β-Thalassemias | NEJM
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
Introductory Chapter: β-Thalassemia | IntechOpen
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
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Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
